Spinal Muscular Atrophy Management Market: By Type of Disease (Type-I, Type-II, Type-III, Type-IV), By Management (Gene Therapy, Drugs), By Distribution Channel (Hospital Pharmacies, Retail Pharmacies, Others) and Geography     

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Spinal Muscular Atrophy Management Market was valued at USD 1.3 Billion in 2020 and is anticipated to grow at USD 2.79 Billion till 2027 recording a CAGR of 11.5% during the forecast period 2021-2027. Spinal muscular atrophy management is a category of hereditary illnesses that causes muscle degradation and compromises muscle function. It usually causes weakness and might even result in death. Motor neurons in the brain and spinal cord are affected by SMA. These motor neurons transmit electric and chemical impulses to and from voluntary muscles in the body, allowing for a variety of physical tasks such as walking, crawling, swallowing, and so on. Spinal muscular atrophy (SMA) management market is at the initial stage. Only one drug was approved for the management (as of 2016) and many of the drugs are still in clinical development. Market players are actively focusing on the drug development to enter into the market. For instance, big players such as Novartis AG is developing drug LMI070, which is in phase 2 clinical trial for management of spinal muscular atrophy type-1. Furthermore, companies are also focusing on acquisitions and mergers for expansion of their developmentl product portfolio. For instance, in January 2015, F. Hoffmann-La Roche AG acquired Trophos, a company focusing on development of novel drugs for orphan and neurodegenerative diseases. By this acquisition, Roche seeks to expand its development portfolio with olesoxime, spinal muscular atrophy drug being developed in phase-II clinical trials. In May 2017, Cytokinetics, Inc.’s pipeline spinal muscular atrophy drug candidate, CK-2127107 got orphan drug designation by Office of Orphan Products Development of U.S. FDA. In December 2016, Biogen Inc. received U.S. FDA approval for SPINRAZA (nusinersen) and European Commission (EC) granted market authorisation for the same in June 2017.    

Spinal Muscular Atrophy Management Market Summary

Study Period


Base Year




Largest Market

North America

Fastest Growing Market

Spinal Muscular Atrophy Management Market Dynamics

Spinal Muscular Atrophy (SMA) is also known as 5q spinal muscular atrophy or autosomal recessive proximal spinal muscular atrophy is a genetic disease affecting the part of nervous system which controls the muscle movement. Spinal muscular atrophy is a rare disorder of neuromuscular system characterised by the progressive muscle wasting, loss of motor neurons, and sometimes may lead to death. There are several types of spinal muscular atrophies are described based on age and accompanying clinical features appearance. The most common types are acute infantile (Type-1), chronic infantile (Type-2), chronic juvenile (Type-3) and adult onset (Type-4) forms. The genetic defects associated with SMA type 1-3 are based on chromosome 5q11.2-13.3.

Key Features of the Reports

  • The report provides granular level information about the market size, regional market share, historic market (2018 to 2022) and forecast (2023 to 2029)
  • The report covers in-detail insights about the competitor’s overview, company share analysis, key market developments, and their key strategies
  • The report outlines drivers, restraints, unmet needs, and trends that are currently affecting the market
  • The report tracks recent innovations, key developments and startup’s details that are actively working in the market
  • The report provides plethora of information about market entry strategies, regulatory framework and reimbursement scenario
  • The report analyses the impact of socio-political environment through PESTLE Analysis and competition through Porter’s Five Force Analysis in addition to recent technology advancements and innovations in the market

Spinal Muscular Atrophy Management Market Segmentation

By type of disease
  • Type-I
  • Type-II
  • Type-III
  • Type-IV
By Management
  • Gene Therapy
  • Drugs
Distribution Channel
  • Hospital Pharmacies
  • Retail Pharmacies
  • Others
North America
  • US
  • Canada
  • Germany
  • France
  • UK
  • Italy
  • Spain
  • Russia
  • Poland
  • Rest of Europe
  • Japan
  • China
  • India
  • Australia & New Zealand
  • ASEAN (Includes Indonesia, Thailand, Vietnam, Philippines, Malaysia, and Others)
  • South Korea
  • Rest of Asia-Pacific
Latin America
  • Brazil
  • Mexico
  • Argentina
  • Venezuela
  • Rest of Latin America
Middle East and Africa (MEA)
  • Gulf Cooperation Council (GCC) Countries
  • Israel
  • South Africa
  • Rest of MEA

Frequently Asked Questions

2021 is the base year and 2028 is the forecast year.

The report covers the five regions and 15+ countries market data: North America (United States, Canada), Europe (Germany, France, Italy, Spain, and United Kingdom (UK), Asia Pacific (China, India, Japan, Australia & New Zealand), Latin America (Brazil, Mexico, Argentina) and Middle East and Africa (Saudi Arabia, United Arab Emirates, South Africa).

In our report, we provide 12-15 market players’ information into the report. However, based on the client’s request we will provide additional country and regional market players information as well.

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  • Astellas Pharma Inc
  • Novartis AG
  • Avexis Inc
  • Biogen
  • F. Hoffmann-La Roche AG
  • Abbot Laboratories
  • Leadiant Biosciences
  • Novo Nordisk A/S