Spinal Muscular Atrophy (SMA) Treatment Market: By Treatment (Gene Therapy, ), Route of Administration (Oral, Intrathecal), Disease Type (Type 1, Type 2, Type 3, Type 4) and Geography

 

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Spinal Muscular Atrophy (SMA) Treatment Market size was valued at USD 2.22 billion in 2021 and is expected to reach USD 13.11 billion by 2028, at a CAGR of 28.9% during the forecast period 2022-2028. Due to increase in awareness regarding the disease (SMA), increase in the research for the rare disease treatment, initiative by government and private organizations to create awareness about the disease SMA, increase in number of initiatives for the treatment procedures of rare diseases, innovation of drugs and other therapies for the treatment and complex nature of the disease are the major factors that are driving the growth of the global spinal muscular atrophy (SMA) treatment market over the forecast timeframe. This report studies global spinal muscular atrophy (SMA) treatment market dynamics elaborately to indentify the current trends & drivers, future opportunities and possible challenges to the key stakeholders operating in the market. In addition, global spinal muscular atrophy (SMA) treatment market report includes human demographics; regulatory scenario, and competition analysis with vividly illustrated the competition dashboard to assess the market competition. Moreover, PBI analyzed global spinal muscular atrophy (SMA) treatment market to better equip clients with possible investment opportunities across the regions (regional Investment Hot-Spots) and market unmet needs (Product Opportunities).

Spinal Muscular Atrophy Sma Treatment Market Summary

Study Period

2023-29

Base Year

2022

CAGR

28.9%

Largest Market

Asia-Pacific

Fastest Growing Market

North-America
Spinal Muscular Atrophy (SMA) Treatment Market Dynamics

Increase in the approval of orphan drugs especially in spinal muscular atrophy (SMA) and growing number of R&D activities for the orphan drugs are the factors that drive the growth of market. For instance, in 2017, USFDA granted an orphan drug license for the treatment of spinal muscular atrophy that is RG7916 which is a development programme by Roche, SMA foundation, and PTC therapeutics. These approvals are expected to increase the research in the field of orphan drugs and are anticipated to propel the global spinal muscular atrophy (SMA) treatment market over the forecast years.

Key Features of the Reports

  • The report provides granular level information about the market size, regional market share, historic market (2017-2021) and forecast (2022-2028)
  • The report covers in-detail insights about the competitor’s overview, company share analysis, key market developments, and their key strategies
  • The report outlines drivers, restraints, unmet needs, and trends that are currently affecting the market
  • The report tracks recent innovations, key developments and startup’s details that are actively working in the market
  • The report provides plethora of information about market entry strategies, regulatory framework and reimbursement scenario
  • The report analyses the impact of socio-political environment through PESTLE Analysis and competition through Porter’s Five Force Analysis in addition to recent technology advancements and innovations in the market

Spinal Muscular Atrophy Sma Treatment Market Segmentation

By Treatment
  • Gene Therapy
  • Drug
Route Administration
  • Oral
  • Intrathecal
By Disease type
  • Type 1
  • Type 2
  • Type 3
  • Type 4

Frequently Asked Questions

2021 is the base year and 2028 is the forecast year.

The report covers the five regions and 15+ countries market data: North America (United States, Canada), Europe (Germany, France, Italy, Spain, and United Kingdom (UK), Asia Pacific (China, India, Japan, Australia & New Zealand), Latin America (Brazil, Mexico, Argentina) and Middle East and Africa (Saudi Arabia, United Arab Emirates, South Africa).

In our report, we provide 12-15 market players’ information into the report. However, based on the client’s request we will provide additional country and regional market players information as well.

  1. Executive Summary
  2. Global Spinal Muscular Atrophy (SMA) Treatment Market Introduction
    • Global Spinal Muscular Atrophy (SMA) Treatment Market – Taxonomy
    • Global Spinal Muscular Atrophy (SMA) Treatment Market –Definitions
      • By Treatment
      • By Route of Administration
      • By Disease Type
      • By Region
  1. Global Spinal Muscular Atrophy (SMA) Treatment Market Dynamics
    • Drivers
    • Restraints
    • Opportunities/Unmet Needs of the Market
    • Trends
    • Global Spinal Muscular Atrophy (SMA) Treatment Market Dynamic Factors - Impact Analysis
    • Global Spinal Muscular Atrophy (SMA) Treatment Market – Competition Landscape
  2. Global Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025
    • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • Year-over-Year (Y-o-Y) Growth Analysis (%)
    • Market Opportunity Analysis
  3. Global Spinal Muscular Atrophy (SMA) Treatment Market, By Treatment, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • Gene Therapy
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Drug Therapy
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Spinal Muscular Atrophy (SMA) Treatment Market Forecast, By Route Of Administration, 2014 - 2018 and Forecast, 2019 - 2025
    • Oral
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Intrethecal
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Spinal Muscular Atrophy (SMA) Treatment Market Forecast, By Disease Type, 2014 - 2018 and Forecast, 2019 - 2025
    • Type 1
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Type 2
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Type 3
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Type 4
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
  1. Global Spinal Muscular Atrophy (SMA) Treatment Market Forecast, By Region, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • North America
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Europe
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Asia-Pacific
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Latin America
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Middle East and Africa
      • Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
      • Year-over-Year (Y-o-Y) Growth Analysis (%) and Market Share Analysis (%)
      • Market Opportunity Analysis
    • Global Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Region, 2019 - 2025
  2. North America Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • By Treatment, 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Gene Therapy
      • Drug
    • By Route of Administration Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Oral
      • Intrathecal
    • By Disease Type Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Type 1
      • Type 2
      • Type 3
      • Type 4
    • Country Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • US
      • Canada
    • North America Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Country, 2019 - 2025
    • North America Spinal Muscular Atrophy (SMA) Treatment Market Dynamics – Trends
  3. Europe Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • By Treatment, 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Gene Therapy
      • Drug
    • By Route of Administration Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Oral
      • Intrathecal
    • By Disease Type Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Type 1
      • Type 2
      • Type 3
      • Type 4
    • Country Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Germany
      • UK
      • France
      • Spain
      • Italy
      • Russia
      • Poland
      • Rest of Europe
    • Europe Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Country, 2019 - 2025
    • Europe Spinal Muscular Atrophy (SMA) Treatment Market Dynamics – Trends
  4. Asia-Pacific Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • By Treatment, 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Gene Therapy
      • Drug
    • By Route of Administration Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Oral
      • Intrathecal
    • By Disease Type Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Type 1
      • Type 2
      • Type 3
      • Type 4
    • Country Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Japan
      • China
      • India
      • ASEAN
      • Australia & New Zealand
      • Rest of Asia-Pacific
    • Asia-Pacific Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Country, 2019 - 2025
    • Asia-Pacific Spinal Muscular Atrophy (SMA) Treatment Market Dynamics – Trends
  5. Latin America Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • By Treatment, 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Gene Therapy
      • Drug
    • By Route of Administration Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Oral
      • Intrathecal
    • By Disease Type Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Type 1
      • Type 2
      • Type 3
      • Type 4
    • Country Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Brazil
      • Mexico
      • Argentina
      • Venezuela
      • Rest of Latin America
    • Latin America Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Country, 2019 - 2025
    • Latin America Spinal Muscular Atrophy (SMA) Treatment Market Dynamics – Trends
  6. Middle East and Africa Spinal Muscular Atrophy (SMA) Treatment Market Analysis, 2014 - 2018 and Forecast, 2019 - 2025 (Revenue, USD Mn)
    • By Treatment, 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%), and Market Share (%)
      • Gene Therapy
      • Drug
    • By Route of Administration Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Oral
      • Intrathecal
    • By Disease Type Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn), Y-o-Y Growth (%) and Market Share (%)
      • Type 1
      • Type 2
      • Type 3
      • Type 4
    • Country Analysis 2014 - 2018 and Forecast 2019 - 2025 by Revenue (USD Mn) Y-o-Y Growth (%) and Market Share (%)
      • Gulf Cooperation Council (GCC) Countries
      • Israel
      • South Africa
      • Rest of MEA
    • MEA Spinal Muscular Atrophy (SMA) Treatment Market - Opportunity Analysis Index, By Treatment, Route of Administration, Disease Type, and Country, 2019 - 2025
    • MEA Spinal Muscular Atrophy (SMA) Treatment Market Dynamics – Trends
  7. Competition Landscape
    • Strategic Dashboard of Top Market Players
    • Company Profiles (Introduction, Financial Analysis, Route of Administration & Service Offerings, Key Developments, Strategies, and SWOT Analysis)
      • Biogen
      • Ionis Pharmaceuticals, Inc.
      • Hoffmann - La Roche Ltd
      • Avexis, Inc.
      • Novartis AG
      • Cytokinetics, Inc.
      • Voyager Therapeutics
  1. Research Methodology
  2. Key Assumptions and Acronyms
  • Biogen
  • Ionis Pharmaceuticals, Inc.
  • Hoffmann – La Roche Ltd
  • Avexis, Inc.
  • Novartis AG
  • Cytokinetics, Inc.
  • Voyager Therapeutics